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Question

Which research institution led the first in-utero treatment for Spinal Muscular Atrophy (SMA)?

The correct answer is

St. Jude Children’s Research Hospital

Why is the news?

“Scientists Achieve First In-Utero Treatment for Spinal Muscular Atrophy Using Risdiplam”

St. Jude Children’s Research Hospital led the first in-utero treatment for Spinal Muscular Atrophy (SMA) using the oral drug risdiplam. This breakthrough offers hope for early intervention in SMA, a neurodegenerative disorder that begins affecting individuals before birth.

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